Genotype-to-referral OS for AATD gene-editing trials that finds untreated PiZZ patients and qualifies centers before launch.
In vivo base editing therapy for rare genetic lung-liver disease
3.2
In vivo base editing therapy for rare genetic lung-liver disease
Cellgorithm cell therapy platform funding
Biological AI with built-in biodefense
Root-cause thyroid autoimmunity therapies
Biology reasoning layer for drug R&D
IMU immune profiling scale-up
SandboxAQ puts quantitative models into Claude
ParcelBio mRNA launch
vision-restoration biotech
CNS drug pipeline launch